A groundbreaking Cleveland Clinic trial is demonstrating how gene-editing technology could transform the way millions of Americans manage high cholesterol. A Phase 1 clinical trial at Cleveland Clinic ...

A single infusion of an experimental gene-editing drug seemed to reduce LDL long-term in a small trial. The results may point ...

Phase 2 trial results showed an improvement in MASH with no worsening of fibrosis in all treatment groups compared with placebo. The Food and Drug Administration (FDA) has granted Breakthrough Therapy ...

Nipocalimab 15mg/kg improved ClinESSDAI score compared with placebo (treatment difference -2.65; [90% CI, -4.03, -1.28]; P =.002). The Food and Drug Administration (FDA) has granted Breakthrough ...

Eli Lilly said its experimental gene-editing therapy cut LDL, or “bad,” cholesterol by up to 62% in an early-stage trial, ...

A newly developed therapy inspired by bacteria residing within tumors offers a different way to combat cancer by targeting how tumor cells produce energy.

A single jab of a breakthrough gene therapy could reverse hearing loss in people within weeks, according to new research. The cutting-edge therapy improved hearing in children and adults with ...

In a major medical breakthrough, scientists have shown that a one-time gene therapy can sharply lower "bad" cholesterol for at least a year, potentially opening the door to a future where some heart ...

An experimental gene-silencing therapy safely lowered LRRK2 protein levels in an early Parkinson’s trial, but its effect on ...